On November 29, 2011, FightSMA will be sponsoring a dinner at Care for Rare, a workshop in Toronto that will chart a collaborative course for a multi-disease effort. Dr. Alex MacKenzie, co–chair of the FIghtSMA Scientific Advisory Committee, will convene pediatric experts at the Westin Harbour Castle (Toronto), to examine ways that science can penetrate the mysteries of rare diseases. The Care for Rare workshop will mobilize a diverse group of experts for orphan disease therapy to both formulate a generalizable approach for pre-clinical orphan disease treatment development and build a short list of disorders to be pursued. SMA is the primary inspiration for this workshop.
We believe that this is just the beginning of what can be achieved with SMA as the cornerstone of such collaborative efforts!